Medera is a clinical-stage biopharmaceutical company focused on targeting difficult-to-treat and currently incurable diseases ...

The FDA’s accelerated approval pathway plays a vital role, and scrapping it or reversing course on already-approved therapies ...

A combination therapy that adds a recently approved drug to the current standard of care for newly diagnosed acute myeloid ...

A gene transfer approach to treating the bleeding disorder hemophilia B remains safe and effective long-term, as scientists ...

Health secretary Robert F. Kennedy Jr. yesterday appointed a new, smaller vaccine advisory committee at the CDC — just two ...

"FDA approves Capsida’s CAP-003 gene therapy for Parkinson’s" was originally created and published by Pharmaceutical ...

Learn more about the generative AI technology that will be used at the Food and Drug Administration (FDA) to speed up reviews ...

Gene therapies have ridden investor mania to huge valuations but commercialization challenges have pushed market caps to the ...

Since the approval of Luxturna, there has been a wave of gene therapies advancing in clinical trials to treat genetic vision ...

This is a developing news story. Please check back soon for updates. The FDA granted VG801 rare pediatric disease designation ...

With a Trump-driven reduction of nearly 2,000 employees, agency officials view artificial intelligence as a way to speed ...