News

Pharmaceutical Technology on MSN1d
FDA approves Capsida’s CAP-003 gene therapy for Parkinson’s
"FDA approves Capsida’s CAP-003 gene therapy for Parkinson’s" was originally created and published by Pharmaceutical ...
STAT7d
FDA reassures rare disease advocates that ‘being flexible’ is plan for gene therapy
Trump health officials signal eased FDA rules for rare disease gene therapy, but concerns linger over safety, oversight, and ...
GEN - Genetic Engineering and Biotechnology News8d
Cell and Gene Therapy Leaders Tell FDA: “Believe in American Solutions”
Leaders from the world of cell and gene therapy shared their personal stories and policy recommendations in an extraordinary ...
BioPharma Dive7d
FDA meeting gives window into gene therapy field’s angst
Gene therapy experts and advocates warning of the sector’s many challenges found a receptive audience in FDA leadership at a ...
The Manila Times20h
Medera and Novoheart Presented Breakthroughs in Human mini-Heart Platforms and Gene Therapy at ISSCR 2025
Medera is a clinical-stage biopharmaceutical company focused on targeting difficult-to-treat and currently incurable diseases ...
pharmaphorum2d
SpliceBio gathers $135m for eye disease gene therapies
SpliceBio's lead in-house pipeline project is in Stargardt disease, an IRD with no approved therapies that is caused by ...
FDA Will Use AI to Approve Drugs and Devices Faster
Learn more about the generative AI technology that will be used at the Food and Drug Administration (FDA) to speed up reviews ...
BioPharma Dive9d
FDA to use new review tool on Sarepta’s gene therapy work
The company is one of the first to receive a “platform technology designation,” which could speed the review of certain gene ...
Labiotech.eu3d
Can gene therapy treat vision loss?
Since the approval of Luxturna, there has been a wave of gene therapies advancing in clinical trials to treat genetic vision ...